Splicing and the SMN2 'Back-Up' Gene - Spinal Muscular Atrophy UK
Spinraza – TreatSMA
Nusinersen ameliorates motor function and prevents motoneuron Cajal body disassembly and abnormal poly(A) RNA distribution in a SMA mouse model | Scientific Reports
Therapy development for spinal muscular atrophy: perspectives for muscular dystrophies and neurodegenerative disorders | Neurological Research and Practice | Full Text
Spinraza binds to a specifi c sequence in the intron downstream of exon... | Download Scientific Diagram
Spinraza, INN - nusinersen
Glen Report 32.14: New Product — 2'-MOE RNA Phosphoramidites
IJMS | Free Full-Text | Development of the Method for Nusinersen and Its Metabolites Identification in the Serum Samples of Children Treated with Spinraza for Spinal Muscular Atrophy
Oligonucleotides to the (Gene) Rescue: FDA Approvals 2017–2019: Trends in Pharmacological Sciences
Nusinersen (Spinraza®) – Spinal Muscular Atrophy (SMA) | National Institute of Neurological Disorders and Stroke
Frontiers | History of development of the life-saving drug “Nusinersen” in spinal muscular atrophy
Therapy development for spinal muscular atrophy: perspectives for muscular dystrophies and neurodegenerative disorders | Neurological Research and Practice | Full Text
Mechanism of action of nusinersen | Download Scientific Diagram
New Drug Product: Spinraza - MPR
Spinraza: Package Insert - Drugs.com
Frontiers | History of development of the life-saving drug “Nusinersen” in spinal muscular atrophy
Attachment: Product Information: Nusinersen (as heptadecasodium)
How the discovery of ISS-N1 led to the first medical therapy for spinal muscular atrophy | Gene Therapy
nusinersen | Ligand page | IUPHAR/BPS Guide to PHARMACOLOGY
Splicing and the SMN2 'Back-Up' Gene - Spinal Muscular Atrophy UK
IJMS | Free Full-Text | Development of the Method for Nusinersen and Its Metabolites Identification in the Serum Samples of Children Treated with Spinraza for Spinal Muscular Atrophy
How SPINRAZA® (nusinersen) Works | HCP
Nusinersen - Wikipedia
Glen Report 32.14: New Product — 2'-MOE RNA Phosphoramidites
Mechanism of approved therapeutics. (A) Nusinersen regulates splicing... | Download Scientific Diagram
